Health
Gene therapy to the inner retina prevents blindness in mouse model of CLN3 Batten disease – News-Medical.Net
Gene therapy to the inner retina prevented blindness in a mouse model of the neuro-degenerative disorder CLN3 Batten disease.
Reviewed by Emily Henderson, B.Sc.Aug 10 2020
Gene therapy to the inner retina prevented blindness in a mouse model of the neuro-degenerative disorder CLN3 Batten disease. Adeno-associated viral (AAV)-mediated expression of the human CLN3 gene led to significant survival of bipolar cells and pre-served retinal function, as reported in the peer-reviewed journal Human Gene Therapy.
Batten disease is a group of fatal, inherited lysosomal storage disorders that predominantly affect children. The m…
-
Noosa News15 hours agoCrucial step in Sea World helicopter crash investigation set
-
Business15 hours agoWhy Accent, DroneShield, EBR Systems, and Titomic shares are pushing higher
-
Noosa News21 hours agoLocal input into new UN treaty – Proctor
-
Business20 hours agoIs the Qantas share price a buy in the tariff ASX stock market volatility?