Health
‘Gene therapy is a game changer for our son’ – BBC News
A five-month-old becomes the first person in England to receive a drug for a devastating disorder.
By Fergus WalshMedical editor
media captionArthur’s dad says “if this treatment didn’t happen, he wouldn’t be around for very long”
Baby Arthur is just five months old. He has no way of knowing the treatment he is receiving in his right arm is the world’s most costly medicine.
He has a devastating progressive disorder that causes loss of muscle control – but has become one of the first patients to be treated on the NHS with Zolgensma, a gene therapy.
Around 40 children are born with the most severe…
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