Health
NIH-funded study finds gene therapy may restore missing enzyme in rare disease – EurekAlert
A new study published in Nature Communications suggests that gene therapy delivered into the brain may be safe and effective…

WHAT:
A new study published in Nature Communications suggests that gene therapy delivered into the brain may be safe and effective in treating aromatic L-amino acid decarboxylase (AADC) deficiency. AADC deficiency is a rare neurological disorder that develops…
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